Project 2: Patient Supported Approaches to Gene Editing “PASAGE”

The PASAGE Study focuses on gene editing technologies to address a range of genetic conditions, from childhood-fatal diseases to conditions that arise in adulthood. The study aims to gather perspectives from patients, families, clinicians, scientists, and policymakers to understand their views, ethical concerns, clinical hopes, and policy needs regarding prenatal gene editing therapies. Key questions revolve around which conditions should be targeted, who should decide, risk/benefit considerations, and ensuring equitable access to therapies.